Tools to start treating hypophosphatasia at its source

3 steps for starting patients on STRENSIQ

Step 1

Reach out to your local Alexion representative who will help guide you through the prescription fulfillment process and connect you with your support team

Step 2

Your Alexion team will help you identify the necessary forms to submit to PANTHERx Rare, the preferred STRENSIQ specialty pharmacy

Step 3

Work with your patient to enroll in OneSource™—the complimentary, personalized patient support program from Alexion

PRO TIP! To streamline the STRENSIQ fulfillment process, consult your Alexion team for guidance on required documentation prior to submitting any forms from the HCP Starter Kit to the specialty pharmacy.

OneSource™ and PANTHERx Rare provide ongoing, personalized support for patients

OneSource™

Complimentary, personalized patient support offered by Alexion:

  • Insurance coverage support (benefits verification, appeals, and more)

  • Disease information

  • Personalized, ongoing support

  • Community connections

www.AlexionOneSource.com

Phone: (888) 765-4747

PANTHERx Rare

The preferred STRENSIQ specialty pharmacy dispenses STRENSIQ and provides:

  • Insurance coverage support (benefits verification, appeals, and more)

  • Clinical support services

  • Coordination with your patient's insurance company to help with coverage

  • Patient education and counseling, including instructions for self-administration

  • Shipments and ongoing refills

  • 24/7 availability and support

www.pantherxrare.com

Phone: (844) 787-6747

Fax: (844) 787-2527

Email: strensiqrph@pantherxrare.com

What support to expect beyond the first year with STRENSIQ

Alexion is committed to providing you with comprehensive support for managing ongoing treatment with STRENSIQ.

Reauthorizations will depend on your patient's healthcare plan. Preparing for those requirements, including the ones below, may be helpful in preventing disruption in treatment.

For patients enrolled in OneSource™, your Alexion team can help research and provide specific details on what information may be required, such as:

  • Baseline measurements
  • Ongoing measurements and assessments
  • Milestones
  • Treatment response
  • Support for ongoing treatment

PRO TIP!

Minimize disruption in treatment by

  • Planning ahead for lab tests well before the reauthorization deadline
  • Anticipating progress assessments that are necessary for continued coverage
    • If these tests (eg, 6-minute walk test) are not offered in your clinical setting, consider referring patient to a local clinician to complete baseline and progression measurements
  • Setting up a reauthorization target date to prepare necessary documents

See Patient Profiles

Patient Profiles

STRENSIQ® (asfotase alfa) IMPORTANT SAFETY INFORMATION INCLUDING BOXED WARNING & INDICATION

WARNING: HYPERSENSITIVITY REACTIONS INCLUDING ANAPHYLAXIS

Patients treated with enzyme replacement therapies have experienced life-threatening hypersensitivity reactions, including anaphylaxis. Anaphylaxis has occurred during the early course of enzyme replacement therapy and after extended duration of therapy.

Initiate STRENSIQ under the supervision of a healthcare provider with appropriate medical monitoring and support measures. If a severe hypersensitivity reaction (e.g., anaphylaxis) occurs, discontinue STRENSIQ and immediately initiate appropriate medical treatment, including use of epinephrine. Inform patients of the symptoms of life-threatening hypersensitivity reactions, including anaphylaxis and to seek immediate medical care should symptoms occur [see Warnings and Precautions (5.1)].

STRENSIQ® (asfotase alfa) IMPORTANT SAFETY INFORMATION INCLUDING BOXED WARNING & INDICATION

WARNING: HYPERSENSITIVITY REACTIONS INCLUDING ANAPHYLAXIS

Patients treated with enzyme replacement therapies have experienced life-threatening hypersensitivity reactions, including anaphylaxis. Anaphylaxis has occurred during the early course of enzyme replacement therapy and after extended duration of therapy.

Initiate STRENSIQ under the supervision of a healthcare provider with appropriate medical monitoring and support measures. If a severe hypersensitivity reaction (e.g., anaphylaxis) occurs, discontinue STRENSIQ and immediately initiate appropriate medical treatment, including use of epinephrine. Inform patients of the symptoms of life-threatening hypersensitivity reactions, including anaphylaxis and to seek immediate medical care should symptoms occur [see Warnings and Precautions (5.1)].

WARNINGS AND PRECAUTIONS

  • Life-threatening Hypersensitivity Reactions, Including Anaphylaxis, have been reported in STRENSIQ-treated patients. Signs and symptoms consistent with anaphylaxis included difficulty breathing, choking sensation, nausea, periorbital edema, and dizziness. These reactions have occurred within minutes after subcutaneous administration of STRENSIQ and have been observed more than 1 year after treatment initiation. Other hypersensitivity reactions have also been reported in STRENSIQ-treated patients, including vomiting, fever, headache, flushing, irritability, chills, erythema, rash, pruritus, and oral hypoesthesia. Consider the risks and benefits of re-administering STRENSIQ following a severe reaction. If the decision is made to re-administer, monitor patients for a reoccurrence of signs and symptoms of a severe hypersensitivity reaction.

  • Lipodystrophy: Localized lipodystrophy, including lipoatrophy and lipohypertrophy has been reported at injection sites after several months in patients treated with STRENSIQ in clinical trials. Advise patients to follow proper injection technique and to rotate injection sites.

  • Ectopic Calcifications: Patients with HPP are at increased risk for developing ectopic calcifications. Events of ectopic calcification, including ophthalmic (conjunctival and corneal) and renal (nephrocalcinosis, nephrolithiasis), have been reported in the clinical trial experience with STRENSIQ. There was insufficient information to determine whether or not the reported events were consistent with the disease or due to STRENSIQ. No visual changes or changes in renal function were reported resulting from the occurrence of ectopic calcifications.


    Ophthalmology examinations and renal ultrasounds are recommended at baseline and periodically during treatment with STRENSIQ to monitor for signs and symptoms of ophthalmic and renal ectopic calcifications and for changes in vision or renal function.

  • Possible Immune-Mediated Clinical Effects: In clinical trials, most STRENSIQ-treated patients developed anti-asfotase alfa antibodies and neutralizing antibodies which resulted in reduced systemic exposure of asfotase alfa. In postmarketing reports, some STRENSIQ-treated patients with initial therapeutic response subsequently developed recurrence and worsening in disease-associated laboratory and radiographic biomarkers (some in association with neutralizing antibodies) suggesting possible immune-mediated effects on STRENSIQ’s pharmacologic action resulting in disease progression. The effect of anti-asfotase alfa antibody formation on the long-term efficacy of STRENSIQ is unknown. There are no marketed anti-asfotase alfa antibody tests. If patients experience progression of HPP symptoms or worsening of disease-associated laboratory and imaging biomarkers after a period of initial therapeutic response to STRENSIQ, consider obtaining anti-asfotase alfa antibody testing by contacting STRENSIQ Medical Information at Alexion at 1-888-765-4747 or by email at medinfo@alexion.com. Close clinical follow up is recommended.

ADVERSE REACTIONS

  • In clinical trials, the most common adverse reactions (≥ 10%) reported were injection site reactions (63%), lipodystrophy (28%), ectopic calcifications (14%), and hypersensitivity reactions (12%). Possible immune-mediated clinical effects have been identified during post-approval use of STRENSIQ.

DRUG INTERACTIONS

Drug Interference with Laboratory Tests:
  • Laboratory tests utilizing alkaline phosphatase (ALP) as a detection reagent could result in erroneous test results for patients receiving treatment due to the presence of asfotase alfa in clinical laboratory samples. Inform laboratory personnel that the patient is being treated with STRENSIQ and discuss use of an alternative testing platform which does not utilize an ALP-conjugated test system.

  • Elevated serum ALP measurements detected through clinical laboratory testing are expected in patients receiving STRENSIQ due to circulating concentrations of asfotase alfa. Do not rely on serum ALP measurements for clinical decision making in patients treated with STRENSIQ.

SPECIAL POPULATIONS

  • Pregnancy & Lactation: There are no available data on STRENSIQ use in pregnant women, the presence of STRENSIQ in human milk, or the effects on the breastfed infant or on milk production, to inform a drug associated risk.

To report SUSPECTED ADVERSE REACTIONS, contact Alexion Pharmaceuticals, Inc. at 1-844-259-6783 or FDA at 1-800-FDA-1088 or www.fda.gov/medwatch.

INDICATION

STRENSIQ® (asfotase alfa) is indicated for the treatment of patients with perinatal/infantile- and juvenile-onset hypophosphatasia (HPP).

Please see full Prescribing Information for STRENSIQ (asfotase alfa), including Boxed WARNING regarding hypersensitivity reactions including anaphylaxis.